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Gene therapy

Researchers are working on new treatments for illnesses caused by changes in genes. One way to do this is using gene therapy. This technique, still in its infancy, aims to provide the body with a new gene to make a protein that is missing or damaged. Gene therapy may eventually be used to treat genetic conditions such as cystic fibrosis, as well as some types of cancer. The main challenge for researchers is getting enough of the gene to the right cells in the body.

Gene therapy aims to provide the body with a new gene to make a protein that is missing or damaged

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